Klotho is advancing its ALS gene therapy candidate KLTO‑202 to the manufacturing phase, and is planning the first human ...

The FDA granted orphan drug designation to Sineugene Therapeutics' SNUG01, a first-in-class experimental gene therapy for ...

Clene is continuing to work with U.S. regulators on its plans to seek accelerated approval of CNM-Au8 for the treatment of ...

A Q&A with author and activist Mindy Uhrlaub, who shares how she is using her voice to raise awareness and support for the ...

As her husband's ALS journey extends, columnist Kristin Neva considers finally "settling in," so to speak, by securing a better bed.

My husband had stage 4 lymphoma, and I was his primary caregiver. My son had kind of gone off the rails and had to be sent to a residential facility for school, and my mom was dying of ALS, ...