使用病毒载体将正常基因输送给因先天性胆碱乙酰转移酶 (ChAT) 基因缺陷而导致严重运动和呼吸障碍的儿童。 冲击 治疗婴儿不治之症，并可能改善胆碱能系统缺陷的神经退行性疾病（如阿尔茨海默病和帕金森病）的症状。 主要拟议活动 改进携带人类 ChAT 基因的 ...

自闭症谱系障碍 (ASD) 是一种复杂的神经发育疾病，影响着美国约 1% 的儿童。 此类疾病的主要特征是言语交流缺陷、社交互动受损、兴趣和行为有限且重复。 原因和最佳治疗方法仍不确定。 ASD 研究的主要障碍之一是缺乏相关的人类疾病模型。 体细胞重编程至多 ...

本次申请请求 (RFA) 的目的是征集高素质的申请人来开发和管理 2017 年年会，以支持 CIRM SPARK 计划。 SPARK 计划为代表该州人口多样性的加州高中生提供在领先的干细胞研究所进行干细胞研究的暑期实践培训机会。 SPARK 会议为期 1 天（加上前一天晚上的晚间社交 ...

我们建议开发间充质干细胞衍生的细胞外囊泡（MSC-EV）作为肺纤维化的治疗方法 据估计，加州有 7000 多人患有特发性肺纤维化 (IPF)，这是一种无法治愈的致命疾病。 目前的治疗只能减缓疾病进展，但不能治愈 IPF。 其中许多人接受肺移植，费用非常昂贵，最多 ...

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The statewide network is designed to overcome manufacturing bottlenecks that have delayed or stalled development and approval of regenerative medicines. “These awards are a critical first step in ...

San Diego, CA – A promising treatment for patients with spinal cord injuries and a therapy aimed at helping HIV patients create an AIDS-resistant blood system were approved today by the state’s stem ...

CIRM’s core programs focus on critical areas that drive the development and commercialization of regenerative medicine treatments. Spanning education, research, and funding opportunities, these ...

Members of the public who are listening to the meeting and wish to make a comment will have the opportunity to do so by doing the following: Once we have called for public comment, members of the ...

Learn more about CIRM’s dedicated board members, how they’re appointed, and the regulations that guide their work. Subcommittees and task forces are comprised solely of board members. They help the ...

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In addition to providing funding for regenerative medical research, CIRM offers a rich array of other resources designed to support and accelerate individual projects. In doing so, CIRM fosters ...